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Generation of two induced pluripotent stem cell lines from a patient with dominant PRPF31 mutation and a related non-penetrant carrier
Journal article   Open access   Peer reviewed

Generation of two induced pluripotent stem cell lines from a patient with dominant PRPF31 mutation and a related non-penetrant carrier

S. McLenachan, D. Zhang, X. Zhang, S-C Chen, T. Lamey, J.A. Thompson, T. McLaren, J.N. De Roach, S. Fletcher and F.K. Chen
Stem Cell Research, Vol.34
2018
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Abstract

We report the generation of the human iPSC line LEIi008-A from a patient with retinitis pigmentosa-11 caused by a dominant nonsense mutation in the PRPF31 gene (NM_015629.3:c.1205C > A p.(Ser402Ter)). A second line, LEIi009-A, was generated from a related non-penetrant carrier of the same mutation with no retinal disease. Reprogramming of patient dermal fibroblasts using episomal plasmids containing OCT4, SOX2, KLF4, L-MYC, LIN28, shRNA for p53 and mir302/367 microRNA generated cell lines displaying pluripotent stem cell marker expression, a normal karyotype and the capability to differentiate into the three germ layer lineages.

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Collaboration types
Domestic collaboration
Citation topics
1 Clinical & Life Sciences
1.36 Ophthalmology
1.36.212 Genetic Retinopathies
Web Of Science research areas
Biotechnology & Applied Microbiology
Cell & Tissue Engineering
Cell Biology
ESI research areas
Molecular Biology & Genetics
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