Leon Larcher

Postdoctoral Scientist, Personalised Medicine Centre, Health Futures Institute, Murdoch University

genetic mutations

C9ORF72 gene

antisense therapeutics

Amyotrophic Lateral Sclerosis

splice-switching

antisense oligonucleotide

organoids

grant | 2025 - 2026

Functional and Transcriptomic analysis of Antisense Oligomer Mediated Modulation of C9ORF72 variant expression

Perron Institute for Neurological and Translational Science

Grant no. 22763.